Pompe disease is a rare ailment, and large pharmaceutical companies have little interest in developing so-called "orphan drugs" for what would be a small market.
「龐貝氏症」是罹病人口稀少的罕見疾病，大藥廠對於這種俗稱「孤兒藥」、市場規模十分有限的藥品研發興趣不大。