Henceforth, the more than 1000 infants born worldwide every year with Pompe disease will no longer face the prospect of death before reaching their first birthdays for lack a treatment for the condition.
從今以後，全球每年誕生的上千位龐貝氏症兒，將不再上演求藥無門、活不過一歲的人倫悲劇。