In simple terms, gene therapy uses techniques from molecular biology to insert healthy genes, directly or indirectly, into human cells, so as to remedy problems caused by defective genes.
簡單地說，基因治療便是利用分子生物學的技術，將正常的基因直接或間接的送入細胞中，以更正修補錯誤的基因，讓它恢復正常。